Sarepta Closes Enrollment in Elevidys Phase 3 Trial, Leaving Non-Ambulatory Duchenne Patients Dependent on a 25-Person Safety Study
· techtimes.com · popularity 20/100 · 0 similar stories today

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Summary
Sarepta ends ENVISION after three Elevidys deaths. Non-ambulatory Duchenne patients now depend on a 25-person sirolimus safety study and Q1 2027 FDA engagement.
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